Our cells rely on microscopic highways and specialized protein vehicles to move everything—from positioning organelles to ...

In a study published in Nature Communications, researchers at the University of Wisconsin–Madison introduced a deep learning ...

This study proposes a new mechanism by which Chd1 senses and responds to DNA unwrapping via EDBL engagement to suppress ...

Huntington's disease is a genetic disorder that kills nerve cells in the brain, causing people to lose their cognitive and ...

An experimental drug known as ulefnersen has shown remarkable efficacy in treating a rare, aggressive form of ALS ...

When Columbia neurologist and scientist Neil Shneider speaks to his ALS patients who volunteer for experimental therapies, he's unwaveringly honest.

Using the gene scissors CRISPR and stem cells, researchers have managed to identify a common denominator for different gene mutations that all cause the neurological disease ALS. The research shows ...

Developed by Sarepta Therapeutics, Elevidys is a one-time, intravenous treatment that uses adeno-associated virus (AAV) ...

Northwestern scientists developed a nanofiber therapy that halts toxic protein clumping in diseases like Alzheimer’s and ALS.

Using the gene scissors CRISPR and stem cells, researchers at Stockholm University and the UK Dementia Research Institute (UK DRI) at King's College London have managed to identify a common ...