Other forms get worse very slowly, and can take 50 or 60 years to progress. This form of muscular dystrophy is actually a group of related conditions. It usually starts in childhood or during the ...
Nila Morton was born with a rare form of muscular dystrophy called Ullrich, which requires her to rely on a wheelchair Nila Morton was born with a rare form of muscular dystrophy called Ullrich ...
Scientists have discovered how to overcome the genetic defect that causes the most serious form of muscular dystrophy, it was revealed today. Although at an early stage, the research may lead to ...
Duchenne muscular dystrophy (DMD) is a rare hereditary disease that is associated with progressive muscle wasting. The ...
The most common form of muscular dystrophy in children is Ducheene dystrophy. This mainly affects boys - one in every 35,000 boys will be born with this form of the disease. It is usually ...
The three-horse race to treat a devastating form of muscular dystrophy is now down to two. One of the key players, Avidity ...
FSHD is the second most common form of muscular dystrophy after the Duchenne type, and affects around 1 million people worldwide, with no approved treatments. It tends to cause muscle wasting in ...
he petitioners are children suffering from several rare diseases, including Duchenne Muscular Dystrophy (DMD) and Mucopolysaccharidosis II or MPS II (Hunter Syndrome). They have sought a direction ...
Chris Anselmo, who has a rare form of muscular dystrophy, hopes to educate pharma on the patient journey and help new patients cope with a life-changing diagnosis. We spoke to him to find out more.