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To help neurologists, clinicians and families understand the current evidence for a new gene therapy for Duchenne muscular ...
Scientists present current evidence for a new gene therapy for Duchenne muscular dystrophy called delandistrogene moxeparvovec.
Chronic muscle inflammation in Duchenne muscular dystrophy (DMD) is driven by both infiltrating and resident macrophages, the latter stimulated by CSF-1 produced by fibro/adipogenic progenitors.
To help neurologists, clinicians and families understand the current evidence for a new gene therapy for Duchenne muscular dystrophy called delandistrogene moxeparvovec, the American Academy of ...
An oral presentation will focus on the treatment of Hemophilia A while new data in the poster session targets the treatment of Duchenne Muscular Dystrophy ... not imply any form of partnership ...
A new study led by researchers at Hospital for Special Surgery (HSS) suggests that currently available therapies may help control chronic muscle inflammation in Duchenne muscular dystrophy (DMD ...
Duchenne muscular dystrophy (DMD), recognised by the World Health Organization (WHO) as a rare disease, is the most common form of childhood muscular dystrophy. It is a progressive genetic ...
Health Secretary Neil Gray has been furiously condemned for failing to ensure access to a new muscular dystrophy drug for desperate children. About 30 boys with a rare form of the killer disease ...
For more than 25 years, Victor has studied DMD and a less aggressive but debilitating variant called Becker muscular dystrophy. This form of muscular dystrophy, usually diagnosed in early adulthood, ...
Chris Anselmo, who has a rare form of muscular dystrophy, hopes to educate pharma on the patient journey and help new patients cope with a life-changing diagnosis. We spoke to him to find out more.
A new study led by researchers at the Hospital for Special Surgery (HSS) suggests that currently available therapies may help control chronic muscle inflammation in Duchenne muscular dystrophy ...