FSHD is the second most common form of muscular dystrophy after the Duchenne type, and affects around 1 million people worldwide, with no approved treatments. It tends to cause muscle wasting in ...

Mitigation specialist Debbie Gaynes has submitted a report that says Lewis has a form of muscular dystrophy that causes cognitive and physical disabilities. Lewis always took special education ...

Pittie’s deeply personal work reflects her reality as a woman with a progressive form of muscular dystrophy. Her Be in Softness contains more than 240 knit vessels, each containing a handwritten ...

Local intramuscular administration of the antisense oligonucleotide PRO051 in patients with Duchenne's muscular dystrophy with relevant mutations was previously reported to induce the skipping of ...

We hypothesize that Duchenne muscular dystrophy and autism spectrum disorder/pervasive developmental disorder co-occur with a greater than random frequency. In this study, we set out to reject the ...

The patient had DMD diagnosed when he was 5.5 years of age and had been treated over the course of 21 years with daily deflazacort (1.1 mg per kilogram per day). He lost the ability to ambulate ...

Pediatric neurologist Omer Abdul Hamid is one of the few doctors in the US who administer gene therapy for Duchenne muscular ...

Pfizer has axed trials of its domagrozumab antibody for Duchenne muscular dystrophy (DMD), after it failed against efficacy targets. Pfizer has been evaluating domagrozumab under the codename PF ...

"I'm so happy because I thought he wasn't going to make it," Taevion Norris' mother said at the graduation ceremony.

Former President Joe Biden has been diagnosed with an “aggressive form” of prostate cancer, one that has spread to his bones. Biden, 82, and his family are reviewing treatment options with his ...

DG9-PMO significantly boosts dystrophin restoration and cardioprotection, addressing a key challenge in the therapy of Duchenne muscular dystrophy.

During REM sleep, the body enters a state of paralysis. This can pose a danger for patients with weakened diaphragms due to neuromuscular diseases. Now new research published at the ATS 2025 ...