Lovina turned 54 years old on May 22. Her children decided to write a tribute column for her. Each child will write a few ...

Families began receiving calls from doctors last week to arrange treatments for new Givinostat drug after a campaign by the ...

gstt.sthames.nhs.uk Although bladder function is thought to be unaffected in Duchenne muscular dystrophy, 46/88 boys interviewed had urinary problems. Nine underwent video urodynamics, showing in ...

Delandistrogene moxeparvovec, a gene therapy for Duchenne muscular dystrophy (DMD), showed high dystrophin expression and a ...

Objective The relationship between functional dependence and quality of life (QOL) in Duchenne muscular dystrophy (DMD) patients and burden and QOL in caregivers is not clear. This study investigated ...

Developed by Sarepta Therapeutics, Elevidys is a one-time, intravenous treatment that uses adeno-associated virus (AAV) ...

Taevion Norris' senior year was suddenly interrupted in March due to heart failure, forcing him to spend the tail end of his final year of high school in the hospital.

Leah Messeropened up to OK! about rumors the show is ending, her relationship with her former Teen Mom 2costars and an update ...

From the column: "The strength of a society is measured by how it cares for its most vulnerable. If our representatives truly ...

Capricor Therapeutics is seeking FDA approval for CAP-1002, targeting heart function in Duchenne Muscular Dystrophy patients.

Taevion Norris’ senior year was interrupted due to heart failure, but that did not stop him from graduating on time at Lurie ...

Gene therapy could be the newest breakthrough for Duchenne muscular dystrophy. While it may not be a cure, it can give independence to boys diagnosed with DMD.