Two dose levels of a single-administration gene therapy were well-tolerated and led to functional improvements in ambulatory ...

Emma Adair, 22, a student from Crumlin abseiled 120ft down the Europa Hotel in Belfast for charity. But her challenge doesn’t ...

A major trial of a promising gene therapy for Duchenne muscular dystrophy has fallen short, but researchers say the lessons learned could pave the way for better, more effective treatments.

Crumlin woman Emma Adair is pushing herself to new limits in April by taking on two challenges to raise vital funds for ...

The Information Day takes place on Wednesday, 4 June 2025, in Lisburn, Co. Antrim, and is organised by the leading charity ...

Muscular Dystrophy UK is calling on people living with a muscle wasting or weakening condition, their families and carers to ...

Spinal muscular atrophy (SMA) is a disorder affecting the motor neurons—nerve cells that control voluntary muscle movement. These cells are located in the spinal cord. Because the muscles cannot ...

One of the amazing things about our changing seasons is just how fast conditions can change. A chunk of turned-up earth is all that remains of the snowbank that blocked my view when pulling out ...

Becker muscular dystrophy (BMD) is a type of muscular dystrophy, a genetic condition that weakens and damages muscles. It can worsen with age. However, its symptoms are less severe than those of ...

Wave Life Sciences’ experimental treatment for Duchenne muscular dystrophy hit the mark in a mid-stage study, setting the stage for a new therapeutic option for patients with the rare disease.

Credit: Shutterstock / ChiccoDodiFC. The beginning to the year has been eventful in the Duchenne muscular dystrophy (DMD) space, with several trial readouts announced at the Muscular Dystrophy ...

"And that's my worry … that we're not being deliberate." In his new book, AI Valley: Microsoft, Google, and the Trillion-Dollar Race to Cash In on Artificial Intelligence, Rivlin writes about ...