Early research shows that editing expanding trinucleotide repeats halts the lengthening process that causes neurological ...

Broad Institute researchers have developed a way to edit the genetic sequences at the root of Huntington's disease and ...

and other trinucleotide repeat disorders, because such changes in DNA occur naturally in people without disease or who only have mild symptoms. “Not only does this study show for the first time ...

PepGen to focus on development of DM1 programme following 10 mg/kg PGN-EDO51 update: Boston Friday, May 30, 2025, 14:00 Hrs [IST] PepGen Inc, a clinical-stage biotechnology compan ...

Clinical genetics involves the study, counselling and treatment of individuals and families with heritable disorders and ... editing of the pathogenic trinucleotide repeat expansions underlying ...

The defending champion Florida Panthers ousted the Tampa Bay Lightning 6-3 in Game 5, wrapping up a convincing series win that bodes well for their repeat bid. The Panthers, healthy after dealing ...

PepGen Inc. , a clinical-stage biotechnology company advancing the next generation of oligonucleotide therapies, today announced that based on the levels of dystrophin protein measured in the 10 mg/kg ...