New gene therapy improves the life of 18-year-old with Sickle Cell Disease which affects 5,000 New Jersey residents living ...

A Falmouth teen, Jayden Wilsey, is the first to receive gene therapy to treat sickle cell at Boston Children's Hospital.

Sickle cell disease is a genetic blood disorder caused by a single mutation in both copies of a gene coding for beta-globin. Beta-globin forms half of the oxygen-carrying molecule hemoglobin.

Sickle cell disease is a genetic blood disorder caused by a single mutation in both copies of a gene coding for beta-globin. Beta-globin forms half of the oxygen-carrying molecule hemoglobin. This ...

Sickle cell disease is a genetic blood disorder caused by a single mutation in both copies of a gene coding for beta-globin. Beta-globin forms half of the oxygen-carrying molecule hemoglobin.

Beam Therapeutics' investigational modified cell therapy for treating sickle-cell disease has been granted orphan-drug status by the Food and Drug Administration.

Sickle cell disease might seem simple enough ... using another form of CRISPR to swap single nucleotides in the genetic code that enhance HbF production. Both therapies are still in clinical ...

Rates of vaso-occlusive crises were similar with crizanlizumab and placebo among patients with sickle cell disease. Results were at odds with the SUSTAIN trial, which showed a reduction in the ...

An algorithm is helping to reduce the number of unnecessary hospital admissions for children with sickle cell.

Sickle cell conditions are genetic blood disorders that affect haemoglobin, the molecule in red blood cells responsible for carrying oxygen throughout the body. While both sickle cell trait and ...

He was diagnosed in 2024 with the sickle cell trait, which has been linked to the deaths of 14 college football players since 2000, according to the National Registry of Catastrophic Sports ...