The Pediatric Emergency Medicine and Pediatric Hematology/Oncology divisions at MUSC have joined forces to create and test an ...

For the first time in his life, a young New Jersey man is pain-free thanks to a new gene treatment working to cure patients ...

Vertex Pharma's £1.65 million ($2.05 million) gene-editing therapy for sickle cell disease (SCD), Casgevy, has been given the green light for use by the NHS in England under a managed access ...

Race has no biological basis and no effect on the onset or progression of disease.

Pfizer is voluntarily withdrawing its sickle cell disease (SCD) therapy Oxbryta from all world markets after finding an "imbalance" in deaths in its clinical trials programme. It's a blow to the ...

KJ Muldoon came into the world with a genetic time bomb ticking inside him.

In a first-in-human phase 1/2 study in seven patients with sickle cell disease, autologous hematopoietic stem cell lentiviral gene therapy using reduced-intensity conditioning was considered ...

New AI Tool Reveals Single-Cell Structure of Chromosomes -- In 3D May 28, 2025 — In a major leap forward for genetic and biomedical research, scientists have developed a powerful new artificial ...

The advance promises to improve diabetes research and cell-based ... Researchers Identify a Dual Origin of Cells Controlling Puberty and Reproduction May 21, 2025 — Researchers have shown that ...

In a first-in-human phase 1/2 study in seven patients with sickle cell disease, autologous hematopoietic stem cell lentiviral gene therapy using reduced-intensity conditioning was considered ...