ATSN-201 was given regenerative medicine advanced therapy designation to treat X-linked retinoschisis, for which there ...

This blog delves into the rise of rare disease drug approvals and the critical importance of regulatory guidance in shaping ...

TLX101 therapy was efficacious in recurrent high-grade glioma, a type of brain cancer, according to preliminary results from ...

Lexeo Therapeutics’ gene therapy provides a healthy version of the frataxin gene, which is critical for energy production in ...

Odylia Therapeutics event brings together leaders across biotech, pharma, venture capital, patient advocacy, and research ...

Atsena Therapeutics, a clinical-stage gene therapy company focused on using the life-changing power of genetic medicine to reverse or prevent blindness, today announced that the U.S. Food and Drug ...

We recently published a list of the 13 Best Biotech Penny Stocks to Buy According to Hedge Funds. In this article, we are ...

We recently published a list of the 11 Best Penny Stocks to Invest in Under $1. In this article, we are going to take a look ...

The immune system must be able to quickly attack invaders like viruses, while also ignoring harmless stimuli, or allergies ...

Belief BioMed and Takeda China today jointly announced that BBM-H901, has been officially approved by the National Medical ...

The original PROOF-HD trial of pridopidine was negative, but a new analysis showed it has clinically meaningful effects in ...

Belief BioMed (BBM) and Takeda China have announced the receipt of China’s NMPA approval for BBM-H901for treating haemophilia ...