Scientists have developed a cortical organoid model for UBA5-associated encephalopathy, revealing a new way to possibly address developmental defects.

The sensory systems profoundly impact cortical development, establishing and refining neural circuits through ...

May 13, 2025 — Experts are urging people, especially those with existing heart or vascular conditions, to seek medical advice before attempting to lose weight using water-only fasting ...

Rare disease treatment poses distinct challenges for physicians, patients, caregivers, and pharma companies. With many of these conditions lacking approved treatments, the standard care often ...

Pneumonia in the Shadow of COVID-19: Along Came COVID Infectious disease experts describe ways in which COVID pneumonia differs from community-acquired pneumonia and how COVID vaccines may offer ...

develop and commercialize novel RNA-based medicines for the potential treatment of severe and rare genetic neurodevelopmental diseases of the CNS. The company was formerly known as Receptor ...

Haematological diseases are pathological conditions primarily affecting the blood or blood-producing organs. This group of disorders includes, but is not limited to, various types of anaemia ...

Due to their human origin and their ability to serve as a "brain avatar" in vitro, hBO offer a promising platform for preclinical research, including the testing of personalized drugs for ...

GC are used as ‘bridging therapy’ during periods of disease activity; for maintenance treatment, they should be minimised to equal or less than 5 mg/day (prednisone equivalent) and, when possible, ...