To help neurologists, clinicians and families understand the current evidence for a new gene therapy for Duchenne muscular dystrophy called delandistrogene moxeparvovec, the American Academy of ...

Scientists present current evidence for a new gene therapy for Duchenne muscular dystrophy called delandistrogene moxeparvovec.

We're very fortunate where I work in Philadelphia to have a robust pediatric team and also a robust adult-focused care team for muscular dystrophy. And so our ability to have this transition ...

Practical pain relief strategies for people with DMD and their caregivers, covering daily care, medications, and emotional support.

Over the last two decades, the 41-year-old Chilean has spent her days bedridden, suffering from degenerative muscular dystrophy. When she finally loses her ability to speak or her lungs fail ...

Over the last two decades, the 41-year-old Chilean has spent her days bedridden, suffering from degenerative muscular dystrophy. When she finally loses her ability to speak or her lungs fail, she ...