Scientists present current evidence for a new gene therapy for Duchenne muscular dystrophy called delandistrogene moxeparvovec.

Practical pain relief strategies for people with DMD and their caregivers, covering daily care, medications, and emotional support.

A new study led by researchers at Hospital for Special Surgery (HSS) suggests that currently available therapies may help ...

The researchers note this therapy is not a complete ... In the case of limb-girdle muscular dystrophy, muscle deterioration is progressive and young adults lose the ability to walk and normal ...

Cas12Max-based gene editing therapy for Duchenne muscular dystrophy, one of the most severe forms of the inherited muscular dystrophies that affects primarily boys. Huidagene Therapeutics and ...

DISCOVERY is a phase 1, proof-of-concept study evaluating safety and expression of the alpha-sarcoglycan protein after treatment with SRP-9004, an investigational gene therapy for the treatment of ...