Researchers from University College London (UCL) are aiming to develop potential treatments for congenital muscular dystrophy ...

New Gene Therapy Approach Shows Promise for Duchenne Muscular Dystrophy July 24, 2024 — Researchers have made a significant breakthrough in developing a new gene therapy approach that restores ...

John Brandsema, MD, a pediatric neurologist at Children’s Hospital of Philadelphia, speaks with Healio about the importance of early diagnosis of muscular dystrophy.

John Brandsema, MD, a pediatric neurologist at Children’s Hospital of Philadelphia, speaks with Healio about the latest ...

A father will soon take on a half marathon following his five-year-old son’s diagnosis with a muscle-wasting condition, which ...

Multidisciplinary coordination across prescribing teams, nursing, laboratory medicine, finance, and infusion centers is crucial for gene therapy delivery in Duchenne muscular dystrophy (DMD).

Marcos Reyes and Valeria Martínez are in a tough spot, unsure which of their twins should receive the treatment they ...

RFK Jr.'s Health Department shut down an advisory group that recommends how to test newborns for genetic disorders.

When actor Eric Dane revealed his diagnosis of amyotrophic lateral sclerosis (ALS), the world took notice. Novant Health ...

Duchenne Muscular Dystrophy: diagnosis, clinical development and global researchMuscular dystrophy refers to a group of rare, genetic, progressive diseases that primarily affect the body’s muscles, ...

Former Grey’s Anatomy star Eric Dane has disclosed that he’s been diagnosed with amyotrophic lateral sclerosis (ALS), ...

Eric Dane, Aaron Lazar, Stephen Hawking and Roberta Flack were all diagnosed with the neurodegenerative disease, which is ...