“For nearly a decade, Sarepta has been a leader in advancing the treatment of Duchenne muscular dystrophy through ... hours after the end of infusion. If symptoms of infusion-related reactions ...

Chronic illness affects 40 percent of school-aged children. Learn how caregivers can help reduce the stress and depression that can accompany this challenge.

Country music star Alan Jackson said during a Milwaukee concert he'd performed his final road show, a few years after ...

The country star revealed his diagnosis on the TODAY show in 2021, explaining that it was the reason for his balance issues ...

Some patients with a rare form of ALS benefited from an experimental therapy, with biomarker evidence of reduced injury to neurons and even limited functional recovery.

When Columbia neurologist and scientist Neil Shneider speaks to his ALS patients who volunteer for experimental therapies, he ...

When Columbia neurologist and scientist Neil Shneider speaks to his ALS patients who volunteer for experimental ...

The gene therapy landscape has seen a paradigm shift in the last few years, mainly due to the advent of CRISPR gene editing technology. The technology holds unprecedented promise for the treatment of ...

Medera is a clinical-stage biopharmaceutical company focused on targeting difficult-to-treat and currently incurable diseases by developing a range of next-generation therapeutics. Medera operates via ...

Managing pain is an important part of living with Duchenne muscular dystrophy (DMD), a progressive neuromuscular ... your physical and emotional well-being with DMD. Pain with DMD can show up in ...