Delandistrogene moxeparvovec, a gene therapy for Duchenne muscular dystrophy (DMD), showed high dystrophin expression and a ...

I had the pleasure of attending a Netflix event around the WoW documentary The Remarkable Life of Ibelin last year—one that was attended by folks from Muscular Dystrophy UK, a charity that helps fund ...

DMD treatment SAT-3247 was safe and well-tolerated, and showed signs of increasing muscle strength in five adults, Satellos ...

No clinically significant changes were observed on physical examination, in vital signs, or on electrocardiograms ... in patients with Duchenne's muscular dystrophy. No serious adverse events ...

Capricor Therapeutics said on Monday the U.S. Food and Drug Administration (FDA) plans to convene a panel of outside experts before deciding on the company's cell therapy for a heart condition related ...

Satellos Bioscience Inc. (TSX: MSCL, OTCQB: MSCLF) ("Satellos" or the "Company"), a biotech company developing new small molecule therapeutic approaches to improve the treatment of muscle diseases and ...

Duchenne muscular dystrophy (DMD), recognised by the World ... neurologist and epileptologist, Medical Trust Hospital, Kochi, early signs of DMD include delays in walking, toe walking, stiffness ...

Taevion Norris’ senior year was interrupted due to heart failure, but that did not stop him from graduating on time at Lurie ...

Building on its 75-year legacy of progress, MDA is reinforcing its commitment to the ALS community by driving momentum for treatments and expanding access to multidisciplinary care. "Eleanor Gehrig's ...

Florida Gov. Ron DeSantis signed another bunch of bills into law, just a day after giving his signature to the largest batch ...

Meghana Keshavan covers biotech and contributes to The Readout newsletter. Want to stay on top of the science and politics driving biotech today? Sign up to get our biotech newsletter in your inbox.

The FDA ordered a clinical hold on Rocket Pharmaceuticals' Danon disease trial after the adverse event was first disclosed.