Cardiac complications in Duchenne muscular dystrophy (DMD) are the result of cardiac muscle involvement that accompanies the ...

Dystrophin's isoforms are thought to contribute variably to neuropsychiatric disorders, behavioral disorders, and ...

Delandistrogene moxeparvovec, a gene therapy for Duchenne muscular dystrophy (DMD), showed high dystrophin expression and a ...

Sarepta Therapeutics, Inc. (NASDAQ:SRPT), the leader in precision genetic medicine for rare diseases, shared the following ...

Advancements in gene therapy for Duchenne muscular dystrophy (DMD) have improved the outlook for some patients, but further ...

Months after causing safety concerns that led the FDA to hit a related trial with a clinical hold, a phase 2 trial of ...

Capricor Therapeutics is seeking FDA approval for CAP-1002, targeting heart function in Duchenne Muscular Dystrophy patients.

MONTGOMERY, Ala. ( WSFA) - After 40 years of service with Montgomery Fire/Rescue, Chief Miford Jordan is retiring. Miford, a ...

Patient advocacy organizations often bring this up as one of the main stressors that people go through living with lifelong genetic disorder like muscular dystrophy. We try very hard on the ...

Families began receiving calls from doctors last week to arrange treatments for new Givinostat drug after a campaign by the ...

An antisense oligonucleotide demonstrated a favorable safety profile and its disease-halting effect in one patient suggests ...

A rare and fatal form of muscular dystrophy has long posed a devastating diagnosis for children, primarily affecting boys.