Breakthrough gene therapy alleviates Dravet syndrome symptoms in mice without side effects
The new therapy, a collaboration between researchers at the ... so scientists overcame this hurdle by using a protein fusion ...
Nature12y
The hair follicle as a gene therapy target
Figure 1: Diagram of the anagen hair follicle ... a characteristic which could be exploited by in vivo and ex vivo gene therapy to produce molecules other than those involved directly in hair ...
EurekAlert!14d
Breakthrough Dravet syndrome gene therapy in mice brings new hope to families
In a groundbreaking advancement for families grappling with the challenges of Dravet syndrome, a rare and life-altering form ...