Leaders from the world of cell and gene therapy shared their personal stories and policy recommendations in an extraordinary roundtable conducted by the FDA in front of its recently-appointed top ...

Gene therapy experts and advocates warning of the sector’s many challenges found a receptive audience in FDA leadership at a ...

Genome editing technologies such as CRISPR/Cas9, base editing, and prime editing are rapidly transforming our ability to ...

Huntington’s disease affects an estimated 5 to 10 per 100,000 people in most Western countries, with variation by region and ...