About DT-216P2 DT-216P2 is an improved formulation of a GeneTAC ® small molecule designed to specifically target the GAA repeat expansion mutation that is the underlying cause of FA and restore the ...

Researchers have developed a gene editing strategy that can repair the genetic problems that lead to Huntington's disease and Friedreich's ataxia. | Genetics And Genomics ...

Figure 4: Correlation between the size of expanded SCA10 ATTCT repeat and the age of onset. Figure 5: Sca10 is widely expressed in brain regions that are anatomical substrates for ataxia and epilepsy.

CAS Key Laboratory of Magnetic Resonance in Biological Systems, State Key Laboratory of Magnetic Resonance and Atomic Molecular Physics, National Center for Magnetic Resonance at Wuhan, Innovation ...

The defending champion Florida Panthers ousted the Tampa Bay Lightning 6-3 in Game 5, wrapping up a convincing series win that bodes well for their repeat bid. The Panthers, healthy after dealing ...

Early research shows that editing expanding trinucleotide repeats halts the lengthening process that causes neurological disease.