“We are hosting the cure FA soiree on Saturday, June seventh At the Omni Hotel in Oklahoma City, and this event was born out ...

Biogen Canada Inc. is disappointed by INESSS's recommendation against listing SKYCLARYS™ (omaveloxolone), despite its therapeutic potential for individuals living with Friedreich ataxia (FA) — a ...

Introduction: Friedreich ataxia (FA) is a monogenic recessive ataxia caused by reduction of a single mitochondrial protein, frataxin (FXN). Although the name of FA refers to the neurodegenerative ...

Initial Data from the Ongoing, Blinded Phase 1 Single-Ascending Dose Trial Has Demonstrated Favorable Safety and Pharmacokinetics IND Application Submitted to Expand RESTORE-FA Trial to U.S. Sites; ...

Researchers have developed a gene editing strategy that can repair the genetic problems that lead to Huntington's disease and Friedreich's ataxia. | Genetics And Genomics ...

Owen Donoghue, 44, took on the challenge to help eight-year-old Craigshill girl Ella-Rose Kennedy who has Friedreich ataxia – ...

A Columbia woman is putting a spotlight on a rare, degenerative disease, which targets the nervous system and often impairs ...

The S&P 500 rose ~6%, nudging back into positive territory for the year.Confident Investing Starts Here: Easily unpack a ...

There are multiple reasons why your joints may ache. Figuring out the origin of the pain is the first step toward finding the right treatment. If your pain is very bad and you know you’ve had an ...

Broad Institute researchers have developed a way to edit the genetic sequences at the root of Huntington's disease and Friedreich's ataxia.The ...