Friedreich’s ataxia (FA) is a neurodegenerative disease most people have never heard of, and it remains widely misunderstood ...

When he was 19, he was halfway through a tattoo apprenticeship when he was diagnosed with Friedreich's Ataxia ... are affected by its life-altering symptoms. "The doctor told me that I had ...

But all that time, she had been reading up on my symptoms on the internet - and came across Friedreich's Ataxia. She was convinced that is what I had and, sure enough, when the results came back ...

Lexeo Therapeutics’ gene therapy provides a healthy version of the frataxin gene, which is critical for energy production in ...

Stifel analysts said that Lexeo’s data showing reduced size and thickness of the heart’s left ventricle are “supportive of a drug effect” for the company’s gene therapy in Friedreich’s ataxia ...

After getting a green light from the European Commission, Biogen’s Skyclarys is the first approved medicine for the inherited neurological disease Friedreich ... a range of symptoms, including ...

Lexeo Therapeutics Inc. produced more positive interim data from early stage studies of its gene therapy to treat Friedreich’s ataxia cardiomyopathy. The results have prompted the company to continue ...

Genetic analysis beyond the causative variants, and independent of the core clinical symptoms (pyramidal signs versus ataxia), might offer a more pertinent way to approach phenotypic variability.

(Journal of the American College of Cardiology) For Friedreich ataxia cardiomyopathy, treatment with the investigational gene therapy LX2006 was associated with improvements in cardiac biomarkers ...

Thomas Deegan and Declan Murray at a concert in St Nicholas Church of Ireland, Dunlavin, in aid of Friedreich's Ataxia research. Photo: Joe Byrne Luca, Claire and Ethon Grace at a concert in St ...