The Gher family has always had a love and a talent for the performing arts. “I really lived a pretty unaffected life until ...

DelveInsight's Friedreich's Ataxia Market Insights report includes a comprehensive understanding of current treatment ...

About DT-216P2 DT-216P2 is an improved formulation of a GeneTAC ® small molecule designed to specifically target the GAA repeat expansion mutation that is the underlying cause of FA and restore the ...

Researchers have developed a gene editing strategy that can repair the genetic problems that lead to Huntington's disease and Friedreich's ataxia. | Genetics And Genomics ...

Owen Donoghue, 44, set out to raise funds for Ella-Rose Kennedy after she was diagnosed with a debilitating progressive brain ...

Early research shows that editing expanding trinucleotide repeats halts the lengthening process that causes neurological disease.

Broad Institute researchers have developed a way to edit the genetic sequences at the root of Huntington's disease and Friedreich's ataxia.The ...

An Edmond family is on a mission to find a cure. For a decade, Michael Gehr has been battling Friedreich's ataxia, a rare ...

Flynn Mitchell said one the lowest moments of his life was trying to get home safely in his wheelchair in the middle of a ...

Billionaire Graeme Hart's granddaughter Jemima Hawkesby and her friend Flynn Mitchell graduating. She is fundraising to help ...