Owen Donoghue, 44, set out to raise funds for Ella-Rose Kennedy after she was diagnosed with a debilitating progressive brain ...

Broad Institute researchers have developed a way to edit the genetic sequences at the root of Huntington's disease and ...

Researchers have developed a gene editing strategy that can repair the genetic problems that lead to Huntington's disease and Friedreich's ataxia. | Genetics And Genomics ...

Early research shows that editing expanding trinucleotide repeats halts the lengthening process that causes neurological ...

Billionaire Graeme Hart's granddaughter Jemima Hawkesby and her friend Flynn Mitchell graduating. She is fundraising to help ...

An Edmond family is on a mission to find a cure. For a decade, Michael Gehr has been battling Friedreich's ataxia, a rare ...

Flynn Mitchell said one the lowest moments of his life was trying to get home safely in his wheelchair in the middle of a ...

After getting a green light from the European Commission, Biogen’s Skyclarys is the first approved medicine for the inherited neurological disease Friedreich ... a range of symptoms, including ...

Biogen’s Skyclarys is on course to becoming the first approved medicine for the inherited neurological disease Friedreich’s ... that results in a range of symptoms that worsen over time ...

Symptoms of DDK may include slow or awkward ... but usually it is people with multiple sclerosis, Friedreich ataxia and another thing we see it cause is a cerebellum lesion." ...

Two 'common' early symptoms of dementia that are not memory ... but usually it is people with multiple sclerosis, Friedreich ataxia and another thing we see it cause is a cerebellum lesion." ...