Scribe Therapeutics reports positive preclinical data on its novel CRISPR technologies at the 2025 EAS Congress and ASGCT Annual Meeting ...

Scientists present current evidence for a new gene therapy for Duchenne muscular dystrophy called delandistrogene moxeparvovec.

INDIANAPOLIS (WISH) — It’s a devastating diagnosis that changes a child’s life forever, Duchenne muscular dystrophy, or DMD, is a rare and fatal genetic disease that primarily affects boys.

Duchenne muscular dystrophy, which primarily affects those of male sex, is an inherited genetic condition that causes muscle weakness. Symptoms usually appear between the ages of two and four and ...

"Sarepta reports outcomes from trial of Duchenne muscular dystrophy therapy" was originally created and published by Clinical Trials Arena, a GlobalData owned brand.

Most children with this condition lose the ability to walk before their teens, however, there is hope for William as he is ...