Developed by Sarepta Therapeutics, Elevidys is a one-time, intravenous treatment that uses adeno-associated virus (AAV) ...

Scribe Therapeutics reports positive preclinical data on its novel CRISPR technologies at the 2025 EAS Congress and ASGCT Annual Meeting ...

A number of strategies can help to ensure adequate joint care to best manage joint pain and stiffness in Duchenne muscular dystrophy (DMD).

Windsor musicians are set to join forces at a charity open mic night, raising funds to help young people living with a rare muscular disorder.

To help neurologists, clinicians and families understand the current evidence for a new gene therapy for Duchenne muscular ...

Scientists present current evidence for a new gene therapy for Duchenne muscular dystrophy called delandistrogene moxeparvovec.

To help neurologists, clinicians and families understand the current evidence for a new gene therapy for Duchenne muscular ...

To help neurologists, clinicians and families understand the current evidence for a new gene therapy for Duchenne muscular dystrophy ...

The CEO at Nottingham-headquartered Blinds 2go is cycling 300km in 24-hours in a bid to raise an impressive £10,000 for ...

The 17-year-old girl was diagnosed with a neuro attack, which landed her on a wheelchair, but her grit and confidence to ...

The National Institute of Allergy and Infectious Diseases (NIAID) plans to initiate phase 1 clinical trial of Capricor's ...