A Falmouth teen, Jayden Wilsey, is the first to receive gene therapy to treat sickle cell at Boston Children's Hospital.

New gene therapy improves the life of 18-year-old with Sickle Cell Disease which affects 5,000 New Jersey residents living ...

Cell and gene therapy (CGT) represents the pinnacle of biomedical innovation, offering unprecedented potential to treat, ...

KJ Muldoon, a 10-month-old baby, was diagnosed with the genetic disease carbamoyl-phosphate synthetase 1 deficiency after he ...

Scientists at the San Raffaele Telethon Institute for Gene Therapy (SR-Tiget), Milan, have found that gene editing using ...

Machine learning models have seeped into the fabric of our lives, from curating playlists to explaining hard concepts in a ...

In comments posted in response to the Trump administration’s pharma tariff investigation, companies and industry groups ...

Researchers have identified an early postnatal window that allows gene transfer to circulating blood stem cells, advancing ...

This first-in-human trial is testing a highly unconventional method: delivering fat-derived stem cells from the patient ...

In the first part of this series, we explored how early genetic screening and gene therapy transform the lives of newborns ...

Scientists behind a world-first gene therapy reveal how they teamed up with experts across academia and industry to produce a ...

Cell and gene therapies harbor great hopes for biomedicine. They are becoming increasingly important for diseases that are ...