The UNC technology, developed by Pediatrics Professor Chengwen Li, M.D., Ph.D., uses adeno-associated viruses (AAVs) to ferry ...

Ophthalmology Times - ophthalmology news, articles, and events in a timely and accurate manner for members of the ophthalmic ...

Researchers from USask have identified a potential target for eliminating breast cancer cells. The team was led by Dr. Franco ...

In a historic medical breakthrough, a child diagnosed with a rare genetic disorder has been successfully treated with a customized CRISPR gene editing therapy by a team at Children's Hospital of ...

A baby born with a rare and dangerous genetic disease is growing and thriving after getting an experimental gene editing ...

A study published in The New England Journal of Medicine looks at a new CRISPR gene therapy for children with a rare genetic disease. Dr Alena Pance, Senior Lecturer in Genetics, University of ...

Scientists in the US have performed the first personalised gene therapy on a child with a life-threatening rare disease, ...

Treated with an individualized gene-editing therapy that corrects mutations directly on the genome, a patient shows improvement from a rare metabolic disease.

The one-off treatment highlights the promise of a new type of gene editing and the challenges of using it to treat extremely ...

For the first time, doctors have created a customized treatment using the revolutionary gene-editing technique known as ...

KJ Muldoon was born with a devastating medical problem. Racing to solve it, doctors may have launched a 'roadmap' for a new ...

Doctors at CHOP and Penn Medicine successfully used gene editing to treat an infant with a rare disorder in what they're ...