A team of doctors at the Children's Hospital of Philadelphia and Penn Medicine treated a baby with a gene editing technology ...

A team of doctors and scientists have successfully treated a rare genetic condition with the first-ever personalized ...

Doctors at CHOP and Penn Medicine successfully used gene editing to treat an infant with a rare disorder in what they're ...

Scientists in the US have performed the first personalised gene therapy on a child with a life-threatening rare disease, ...

Ask scientists which gene-editing tool is most needed to advance gene therapy, and they'd probably describe a system that's ...

A research team has developed and safely delivered a personalized gene editing therapy to treat an infant with a life-threatening, incurable genetic disease. The infant, who was diagnosed with the ...

In a historic medical breakthrough, a child diagnosed with a rare genetic disorder has been successfully treated with a ...

A baby born with a rare and dangerous genetic disease is growing and thriving after getting an experimental gene editing ...

Metabolic disorders such as argininosuccinic and glutaric aciduria, methylmalonic acidemia, homocystinuria or primary hyperoxaluria require specific diets to prevent the accumulation of substances ...

In a historic medical breakthrough, a child diagnosed with a rare genetic disorder has been successfully treated with a customized CRISPR gene editing therapy by a team at Children's Hospital of ...

The UNC technology, developed by Pediatrics Professor Chengwen Li, M.D., Ph.D., uses adeno-associated viruses (AAVs) to ferry ...

The technique used on a 9½-month-old boy with a rare condition has the potential to help people with thousands of other ...