Victoria Gray is the first person in the world to receive CRISPR,  a gene-editing therapy for sickle cell disease created by ...

By reprogramming brain cells, a new gene therapy approach for Alzheimer's developed by UC San Diego researchers could address ...

While heritable human genome editing is banned in the United States, across Europe and much of the world, the technology ...

Scientists have made a key breakthrough in treating respiratory diseases by developing a new drug delivery system that ...

Interim results from a small group of children in a Phase I/II trial are essentially in line with that of Elevidys, according ...

Congress, convening virtually and in Milan, Italy, from June 12 to June 15, 2025, will feature a revamped program structure ...

Baby KJ Muldoon, the first patient to successfully receive personalized CRISPR gene editing therapy has returned home after over 300 days at the hospital.

Researchers at University of California San Diego School of Medicine have developed a gene therapy for Alzheimer's disease ...

A molecular assay identified patients with non–small cell lung cancer most likely to benefit from adjuvant chemotherapy, ...

Researchers at the University of California San Diego School of Medicine have developed a gene therapy for Alzheimer's ...

A Falmouth teen, Jayden Wilsey, is the first to receive gene therapy to treat sickle cell at Boston Children's Hospital.

Scientists at the San Raffaele Telethon Institute for Gene Therapy (SR-Tiget), Milan, have found that gene editing using ...