A gene editing drug custom-made for a critically ill baby showed that, for some ultra-rare diseases, it’s possible to design ...

In a historic medical breakthrough, a child diagnosed with a rare genetic disorder has been successfully treated with a ...

A tailored CRISPR base-editing therapy was given for the first time to an infant who was born with a rare genetic disease, ...

A Delaware County infant with a rare metabolic disease, CPS1 deficiency, was treated at CHOP with a custom CRISPR therapy.

An infant in Philadelphia has been successfully treated with a customized Crispr gene-editing therapy for a rare and deadly ...

Aldevron and Integrated DNA Technologies – both part of the Danaher Corporation – have achieved a medical milestone with the ...

A baby born with a rare and dangerous genetic disease is thriving after getting an experimental gene editing treatment made ...

Stylus Medicine, a startup founded by Patrick Hsu, has raised $85 million to develop a suite of technologies that it believes ...

The researchers have conducted a first-in-human clinical trial testing a CRISPR/Cas9 gene-editing technique aimed at ...

In a historic medical breakthrough, a child diagnosed with a rare genetic disorder has been successfully treated with a customized CRISPR gene editing therapy by a team at Children's Hospital of ...

CRISPR Therapeutics’ partner Vertex reported that more than 65 treatment centers have been activated for the gene therapy ...

Treated with an individualized gene-editing therapy that corrects mutations directly on the genome, a patient shows improvement from a rare metabolic disease.