You may have seen it in the news recently: a baby in Pennsylvania with a rare genetic disorder was healed with a personalized treatment that repaired ...

The personalized CRISPR treatment could be the future of gene therapy, but hurdles remain before everyone has access.

Intellia has leveraged its expertise in Crispr/Cas9 gene editing to advance a pipeline of in vivo and ex vivo therapies for diseases with high unmet medical needs. We believe Intellia's proprietary ...

Researchers at the Max Planck Institute for Evolutionary Anthropology have addressed a longstanding challenge in CRISPR ...

The birth took place at Sher-e-Kashmir University of Agricultural Sciences and Technology (SKUAST-Kashmir). Officials say it ...

With up to 40%, the point mutation H1069Q is the most common mutation of the Cu transporter ATPase7B in Western populations,” the authors wrote. “The aim of this study was to assess if a ...

CRISPR-Cas9 is one of the biggest discoveries ... This precision reduces the risk of unintended mutations and is particularly useful for correcting point mutations associated with genetic diseases.

Delivered by a virus, CRISPR pulled an ... of most familial AD mutations. Single-nucleus transcriptomic analysis in these mice indicated that their microglia remained in a homeostatic state at 10 ...

This precision reduces the risk of unintended mutations or off-target effects associated with CRISPR-Cas9. Additionally, base editing can efficiently correct point mutations associated with genetic ...

It may seem simple, but a small difference in spelling can create mutations that result in life-threatening diseases. Gene variants that cause genetic diseases come in many varieties. Transition point ...

If someone’s disease was due to a gene mutation or loss ... says the precision allowed by CRISPR-Cas9’s programmability is its singular selling point. “Traditional gene therapy, which ...

Casgevy uses the CRISPR/Cas9 enzyme to mimic this protective genetic mutation. It makes a cut at ... like Woolford, point out that they want to see far-reaching data about that before using ...