Beta-thalassemia: Everyone has two beta globin genes (one on each chromosome 11). The severity depends on how many of these two genes are defective: One gene mutation: Beta-thalassemia minor ...

A Falmouth teen, Jayden Wilsey, is the first to receive gene therapy to treat sickle cell at Boston Children's Hospital.

Geneticists have used a cutting-edge DNA base editing treatment on several patients to cure thalassemia, a prevalent and severe genetic blood disease.

With gene therapy offering new hope for thalassemia, experts urge Indian govt to invest in early diagnosis, genetic testing, ...

Editas Medicine reports successful gene editing levels in stem cells, supporting potential treatment for sickle cell disease and beta thalassemia. Editas Medicine announced promising new data on ...