Their results are described in a Nature Genetics paper published this week titled “Base editing of trinucleotide repeats that ...

Broad Institute researchers have developed a way to edit the genetic sequences at the root of Huntington's disease and ...

A common sleep aid restores healthier sleep patterns and protects mice from the brain damage seen in neurodegenerative ...

Mice genetically engineered to lack the ability to make the amino acid cysteine, and fed a cysteine-free diet, lost 30 percent of their body weight in just one week, a new study shows.

It's a bit Frankenstein in nature, but researchers at NYU Grossman School of Medicine genetically altered mice to stop ...

New studies show that astrocytes, long thought to be support cells in the brain, are crucial intermediaries for relaying messages to neurons.

The lack of animal models that mimic human disease impedes the study of many pathologies that still lack treatment beyond symptom relief. This is what has happened so far with PURA syndrome, a rare ...

Scientists working at the NIH’s BRAIN Initiative have created new viral vectors that one day could lead to gene therapies for ...