A research team led by Professor Choi Byung-yoon of the otolaryngology department at Bundang Seoul National University Hospital (Harvard University researcher Kim Ye-ri, Regeneron Chung Yoo-jin, and ...

Shares of gene therapy developer uniQure N.V. (QURE) shot up 41% on Thursday afternoon after it announced that the U.S. Food and Drug Administration (FDA) has granted Breakthrough Therapy designation ...

Scholar Rock Holding Corporation's apitegromab shows promise for SMA treatment, aims for 2025 launch. Click for my updated ...

Breakthrough Therapy designation based on clinical evidence from Phase I/II trials showing meaningful slowing of disease progression ~~ ...

A multinational research team of clinicians and scientists from South Korea and Singapore has published positive findings ...

Ultragenyx's strong revenue growth, diverse streams, and late-stage pipeline make it a standout in rare disease and gene ...

Learn about Brink Tx as it raises $4 million to go beyond CRISPR with engineered recombinases in CAR T therapy.

In a paper published in MedComm, an international team of scientists provided an overview of the advancements in the ...

Stifel head of biotech research Paul Matteis suggests looking for biotech names not dependent on the FDA while this sector ...

Explore the advancements in stem cell therapy for neurodegenerative diseases. Discover market size, trends, and growth projections for 2035 with a focus on treatment innovations.

Atsena Therapeutics, a clinical-stage gene therapy company focused on using the life-changing power of genetic medicine to reverse or prevent blindness, today announced that the U.S. Food and Drug ...