Scientists at the San Raffaele Telethon Institute for Gene Therapy (SR-Tiget), Milan, have found that gene editing using ...

Researchers have identified an early postnatal window that allows gene transfer to circulating blood stem cells, advancing ...

KJ Muldoon, a 10-month-old baby, was diagnosed with the genetic disease carbamoyl-phosphate synthetase 1 deficiency after he ...

New gene therapy improves the life of 18-year-old with Sickle Cell Disease which affects 5,000 New Jersey residents living ...

Scientists at the San Raffaele Telethon Institute for Gene Therapy (SR-Tiget), Milan, have found that gene editing using ...

With gene therapy offering new hope for thalassemia, experts urge Indian govt to invest in early diagnosis, genetic testing, ...

Cell and gene therapy (C&GT) is set to revolutionise treatment of complex diseases, offering new possibilities for patients.

Thalassemia, a group of inherited blood disorders characterized by reduced or abnormal hemoglobin production, continues to ...

In medical breakthrough, a baby diagnosed with rare genetic disorder is thriving after customized CRISPR gene editing therapy ...

Tumors were permitted to grow to approximately 200 mm^3 before the mice were used in biodstribution or therapy studies ... into an effective anti-tumor immune response. One of the major barriers to ...

gene-editing has taken a major leap toward personalized medicine. As Kiran Musunuru, professor of Translational Research in Penn’s Perelman School of Medicine, put it in a press statement, “The ...

An infant with a life-threatening and incurable genetic disease has become the first human to successfully receive a personalized gene editing therapy. This is a massive achievement and could ...