Joe Jackson’s son, William, is 6 years old and has Duchenne muscular dystrophy, a disease that can claim the lives of boys ...

An infant named KJ has made history as the first patient to be treated with an in vivo CRISPR gene editing therapy designed ...

Duchenne muscular dystrophy (DMD), recognised by the World Health Organization (WHO) as a rare disease, is the most common form of childhood muscular dystrophy. It is a progressive genetic ...

An oral presentation will focus on the treatment of Hemophilia A while new data in the poster session targets the treatment of Duchenne Muscular Dystrophy ... not imply any form of partnership ...

A new study led by researchers at Hospital for Special Surgery (HSS) suggests that currently available therapies may help control chronic muscle inflammation in Duchenne muscular dystrophy (DMD ...

Thousands of patients have been treated with REGENXBIO's AAV Therapeutic platform, including Novartis' Zolgensma® for children with spinal muscular ... not imply any form of partnership ...

About Duchenne Muscular Dystrophy (Duchenne) Duchenne is a form of muscular dystrophy that occurs primarily in males. It causes progressive weakness and loss of skeletal, cardiac, and respiratory ...

Duchenne muscular dystrophy (DMD) is a rare neurological ... DMD can cause a mild form of intellectual disability. This means there may be challenges in how someone with DMD can learn and ...

The Muscular Dystrophy Association (MDA) today celebrates the decision by the US Food and Drug Administration (FDA) to grant approval of a risdiplam (Evrysdi) in tablet form, marking a significant ...

Muscular dystrophy can appear in infancy up to middle age or later, and its form and severity are determined in part by the age at which it occurs. Some types of muscular dystrophy typically ...

He’s being home schooled to complete his senior year of high school and plans to attend college to study technology.

“There were two siblings diagnosed with a form of muscular dystrophy. And their mom was in the room with us and she was very concerned about this diagnosis. And it just reminded me how I felt ...