Explore a comprehensive guide to standardizing large scale production and clarification of lentiviral vectors.

Researchers have demonstrated, for the first time in the world using mice, the ability to overcome significant challenges in ...

Organoids were cultured from healthy donor iPSC sources and differentiated using the human iPSC-derived Cerebral Organoid ...

This article examines viral and non-viral vectors in gene therapy, highlighting their mechanisms, advantages, and limitations ...

Amid a broader push to beef up cell and gene therapy manufacturing capacity in Europe, Novartis has opened the doors to a €40 ...

Prolific Machines, a biotechnology innovator unlocking unprecedented cellular control with light, appoints Christina Perry as CFO.

For the last 10 years, the only effective treatment for hypophosphatasia (HPP) has been an enzyme replacement therapy that must be delivered by injection three-to-six times each week.

"We have essentially titrated the viral vector to show which dose achieves ... late-onset HPP as adults rather than infants, the gene therapy was more effective on female mice, and in females ...

Results show improved functional outcomes for people with Duchenne muscular dystrophy who are ambulatory. Elevidys, which is ...

The findings from this research are expected to be applied as a new therapeutic approach to viral vector treatments, which are currently limited by neutralizing antibodies. Gene therapy is a ...