PHILADELPHIA (WPVI) -- An infant, who was born with a deadly disease, is now thriving, thanks to a medical first performed at ...

In a groundbreaking achievement, doctors have successfully treated a baby boy with a life-threatening genetic disorder using ...

For the first time, doctors have created a customized treatment using the revolutionary gene-editing technique known as ...

Sandra A. Banta-Wright, MN, RNC, NNP; Robert D. Steiner, MD Neonates with profound and prolonged hyperammonemia with coma due to urea cycle defect will have had a neurological insult to the brain ...

The goal is to reuse key parts of the treatment and simply swap in a custom set of instructions for each patient's specific ...

Fargo’s Aldevron helped create a custom gene-editing therapy that cured a baby of urea cycle disorder, a rare and potentially ...

A tailored CRISPR base-editing therapy was given for the first time to an infant who was born with a rare genetic disease, ...

A newborn boy, KJ, was diagnosed at birth with a rare and potentially fatal genetic disease. He received a novel, on-demand CRISPR therapy in record time.

KJ Muldoon was born with a devastating medical problem. Racing to solve it, doctors may have launched a 'roadmap' for a new type of treatment.