Fargo’s Aldevron helped create a custom gene-editing therapy that cured a baby of urea cycle disorder, a rare and potentially ...

The baby boy received the bespoke therapy within a few months of birth and is doing well, according to a presentation at ASGCT.

Sandra A. Banta-Wright, MN, RNC, NNP; Robert D. Steiner, MD Neonates with profound and prolonged hyperammonemia with coma due to urea cycle defect will have had a neurological insult to the brain ...

It is driven by the increasing prevalence of UCDs. The global urea cycle disorder (UCD) treatment market is projected to grow by $215.4m from 2024 to 2028, at a CAGR of 3.2%, according to Technavio.