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GEN - Genetic Engineering and Biotechnology News4d
Base Editors Curb Repeating DNA in Huntington’s and Ataxia Models
Early research shows that editing expanding trinucleotide repeats halts the lengthening process that causes neurological ...
Gene editing disrupts Huntington's mutation in mice
Broad Institute researchers have developed a way to edit the genetic sequences at the root of Huntington's disease and ...
EurekAlert!5d
Gene editing disrupts Huntington’s mutation in mice
and other trinucleotide repeat disorders, because such changes in DNA occur naturally in people without disease or who only have mild symptoms. “Not only does this study show for the first time ...
Pharmabiz3d
PepGen to focus on development of DM1 programme following 10 mg/kg PGN-EDO51 update
PepGen to focus on development of DM1 programme following 10 mg/kg PGN-EDO51 update: Boston Friday, May 30, 2025, 14:00 Hrs [IST] PepGen Inc, a clinical-stage biotechnology compan ...
Nature2d
Large expansion of the ATTCT pentanucleotide repeat in spinocerebellar ataxia type 10
Figure 1: Expansion mutations in four SCA10 families. Figure 4: Correlation between the size of expanded SCA10 ATTCT repeat and the age of onset. Figure 5: Sca10 is widely expressed in brain ...
Le Lézard4d
PepGen to Focus on Development of Promising DM1 Program Following 10 mg/kg PGN-EDO51 Update
PepGen Inc. , a clinical-stage biotechnology company advancing the next generation of oligonucleotide therapies, today announced that based on the levels of dystrophin protein measured in the 10 mg/kg ...
Science Daily3d
Mental Health Research News
May 21, 2025 — A new study confirms that children of people with schizophrenia or bipolar disorder have a higher risk of developing psychopathology compared to ... Good News for People With ...