The investment from Uganda Development Bank supported MHS in acquiring capital-intensive equipment and purchase of raw ...

Researchers are enhancing the best features of AAV capsids and overcoming their limitations to accelerate gene-based therapies.

Su S., Hu, Y., Evolving patterns in a collaboration network of global R&D on monoclonal antibodies, mAB’s, 2017, 9,7, 1041-1051. Vertex's gene-editing therapy for sickle cell disease ...

CytomX’s pipeline currently comprises seven therapeutic candidates across multiple treatment modalities, including antibody-drug conjugates (ADCs), T-cell engaging bispecific antibodies (TCBs ...

A new gene editing treatment has been approved for use in the NHS, which will help treat sickle cell disease patients ...

Sickle cell anaemia is a genetic blood disorder characterised by the production of an abnormal haemoglobin, known as haemoglobin S. Sickle cell disease changes the shape of blood cells into a crescent ...

New gene therapies could transform sickle cell treatment forever. A future without pain crises or hospitalizations may finally be within reach.

NHS approves £1.65m gene therapy for sickle cell disease, offering a potential cure. A milestone for patients, especially in ...

Would the transplant work? What would it look like to have a successful stem cell transplant? Would it be a cure for my sickle cell disease? It was a decision I could think about making because my ...

A sickle cell disease “cure” is to be offered to NHS patients for the first time. The £1.65 million gene therapy called exa-cel, also known under the brand name Casgevy, uses a Nobel Prize ...

January 2025 kicked off with a wave of impactful biotech deals, setting the stage for an exciting year of innovation.

A "groundbreaking" £1.65 million treatment has been approved for use on the NHS, offering patients with severe sickle cell disease some hope of a cure. It is believed around 1,700 people could be ...