Recently approved gene therapies offer patients one-time, potentially curative treatments for genetic diseases such as sickle ...

The Food and Drug Administration has approved the world’s first medicine based on CRISPR gene-editing technology, a ...

Doctors and researchers at the University of Nebraska Medical Center are hoping to bring a different therapy that uses a ...

When even one tiny section of a person’s genetic code becomes mutated or modified, cells can begin to act out of ...

Many high risk, high reward medical therapies that use cutting edge science are proving themselves in clinical trials. But are health services ready to pay for them—and how? Marianne Guenot reports On ...

Gene therapy, with its offer of a possible cure for rare diseases like sickle cell, is losing early investors to ...

Following a breakthrough 'cure' for sickle cell disease being approved on the NHS, the Mirror sat down with four British ...

Calvin Campbell lost all the flesh on his legs and was paralysed for months because of an agonising disease that's the fastest growing genetic condition in the UK ...

The global gene therapy market is projected to grow at a significant CAGR of 20% from 2024 to 2029. This growth is driven by ...

Sickle cell disease affects only adult hemoglobin, causing it to clump and distort red blood cells into a sickle shape. Preserving fetal hemoglobin after birth at levels above 8% through gene editing ...

Vertex Pharma's £1.65 million ($2.05 million) gene-editing therapy for sickle cell disease (SCD), Casgevy, has been given the green light for use by the NHS in England under a managed access ...

the first CRISPR/Cas9 gene-editing therapy in the UAE. This achievement opens new horizons and offers innovative treatment for patients suffering from sickle cell disease (SCD) and transfusion ...