A baby born with a rare and dangerous genetic disease is growing and thriving after getting an experimental gene editing ...

Though it may be a while before similar personalized treatments are available for others, doctors hope the technology can ...

A Delaware County infant with a rare metabolic disease, CPS1 deficiency, was treated at CHOP with a custom CRISPR therapy.

Baby born with rare life-threatening disorder makes medical history - Researchers hope what they learn from KJ will help ...

For the first time, doctors have created a customized treatment using the revolutionary gene-editing technique known as ...

Researchers can target either the coding DNA strand or its complementary partner for ... With another program, Beam is seeking to set itself apart in the sickle cell disease space. Both bone marrow ...

The Michigan Sickle Cell Data Collection Program has been tracking information from the estimated 4,000 Michigan residents ...

Free sickle cell trait screenings are making a difference in Jefferson County where students and health officials say testing ...