“This is the first step towards the use of gene editing therapies to treat a wide variety of rare genetic disorders for which ...

Though it may be a while before similar personalized treatments are available for others, doctors hope the technology can ...

A Delaware County infant with a rare metabolic disease, CPS1 deficiency, was treated at CHOP with a custom CRISPR therapy.

Baby born with rare life-threatening disorder makes medical history - Researchers hope what they learn from KJ will help ...

For the first time, doctors have created a customized treatment using the revolutionary gene-editing technique known as ...

A baby born with a rare and dangerous genetic disease is growing and thriving after getting an experimental gene editing ...

The Michigan Sickle Cell Data Collection Program has been tracking information from the estimated 4,000 Michigan residents ...

Free sickle cell trait screenings are making a difference in Jefferson County where students and health officials say testing ...

Sickle Cell Disease is a chronic, inherited blood disorder that affects millions of people worldwide. It is best known for causing anaemia, pain episodes, and organ complications, but a lesser ...

Medical experts and cultural leaders in the Lango sub-region have proposed various measures to reduce the financial burden of treating Sickle Cell Disease (SCD), following the withdrawal of USAID ...