For the first time in his life, a young New Jersey man is pain-free thanks to a new gene treatment working to cure patients ...

Vertex Pharma's £1.65 million ($2.05 million) gene-editing therapy for sickle cell disease (SCD), Casgevy, has been given the green light for use by the NHS in England under a managed access ...

Pfizer is voluntarily withdrawing its sickle cell disease (SCD) therapy Oxbryta from all world markets after finding an "imbalance" in deaths in its clinical trials programme. It's a blow to the ...

KJ Muldoon came into the world with a genetic time bomb ticking inside him.

Women age differently from men when it comes to health—particularly in conditions like cardiovascular disease and ...

Dr. Simrit Parmar, an associate professor in the College of Medicine at Texas A&M University and founder of the ...

The advance promises to improve diabetes research and cell-based ... Researchers Identify a Dual Origin of Cells Controlling Puberty and Reproduction May 21, 2025 — Researchers have shown that ...

A new study has shown that lowering levels of a protein called EMC10 can restore brain function and memory in models of 22q11.2 Deletion Syndrome, pointing to a potential treatment approach.

Gene Modification Could Improve Cancer Treatment's Success Rate Feb. 7, 2025 — A research team has made a major discovery on how the CUL5 gene affects CAR-T cell therapy, an advanced cancer therapy.

Whole-genome association studies have recently been proposed as a powerful approach for detecting the many subtle genetic effects that underlie susceptibility to common diseases 1,2,3. In contrast ...