Chow is City of Hope’s first sickle cell patient, while a beta thalassemia patient has been treated at Children’s National. Several authorized centers told WIRED they will begin infusions of ...

Exagamglogene autotemcel (exa-cel) (Casgevy®) is a gene therapy for treating sickle cell disease in patients 12 years and older with recurrent vaso-occlusive crises and transfustion-dependent beta ...

Thalassemia is an inherited disease that ... symptoms thalassemia major or Cooley anemia changes on two beta-globin genes sickle trait and changes in the beta-globin gene coinheritance changes ...

"We have about eight patients that are in the insurance approval process," she said, for gene therapy treatments for beta thalassemia and sickle cell disease. "It's something that we do expect to ...

A three-year study by Metropolis Healthcare reveals that 28.4 per cent of nearly 20,000 children screened for ...

Editas Medicine reports successful gene editing levels in stem cells, supporting potential treatment for sickle cell disease and beta thalassemia. Editas Medicine announced promising new data on ...

A new study reveals that over one in four Indian children under 12 carry inherited blood disorders. The findings highlight ...

a CRISPR/Cas9 gene-editing therapy aimed at treating sickle cell disease and transfusion-dependent beta-thalassemia The treatment is provided by Abu Dhabi Stem Cells Center, with the first patient ...