Hydrocortisone oral solution (Khindivi) was approved as a replacement therapy for pediatric patients ages 5 years and up with ...

The Food and Drug Administration (FDA) has accepted for Priority Review the New Drug Application (NDA) for TransCon ® CNP (navepegritide) for the treatment of children with achondroplasia, a rare ...

Shares of Ascendis Pharma A/S (NASDAQ:ASND) climbed 5.8% today after the company announced that the U.S. Food and Drug Administration (FDA) has accepted for priority review its New Drug Application ...

Ascendis Pharma announced that the FDA has accepted its New Drug Application for TransCon CNP, a treatment for children with achondroplasia, for priority review.

TransCon CNP demonstrated significantly higher annualized growth velocity, the primary endpoint, compared to placebo – ...

Shares of Ascendis Pharma AS (NASDAQ:ASND) rose 5.8% after the U.S. Food and Drug Administration (FDA) accepted the company’s ...

Hannah Leonard, who has achondroplasia, a bone growth disorder which causes dwarfism, said she lost working family tax ...

Vladimir Putin had a m Archpriest Alexander Tkachenko, Chairman of the Board of the Circle of Kindness Foundation for ...

A man with dwarfism told The Repair Shop experts they'd given him "freedom" after they restored a rare canoe he could use to ...

Social media users have showed their support and congratulations to the former Team GB swimmer and her new documentary ...

The Team GB swimmer from Swansea delves in to her adoption and whether or not she wants biological children in her new ITV ...

In her latest ITV documentary, the Paralympic champion delves into the morally complicated world of disability and motherhood ...