Timing of the surgery varies and may be dictated by the underlying disorder. In the presence of muscular dystrophy, for example, we consider surgical intervention once the child is wheelchair-bound, ...

A rare and fatal form of muscular dystrophy has long posed a devastating diagnosis for children, primarily affecting boys.

DMD treatment SAT-3247 was safe and well-tolerated, and showed signs of increasing muscle strength in five adults, Satellos ...