A 46-year-old woman with type 1 myotonic dystrophy (DM1) presented to the emergency department with dyspnea and palpitations.

DMD treatment SAT-3247 was safe and well-tolerated, and showed signs of increasing muscle strength in five adults, Satellos ...

gstt.sthames.nhs.uk Although bladder function is thought to be unaffected in Duchenne muscular dystrophy, 46/88 boys interviewed had urinary problems. Nine underwent video urodynamics, showing in ...

Acute myeloid leukemia (AML) can cause many different signs and symptoms. Some are more common with certain subtypes of AML. More often these symptoms are caused by something other than leukemia. But ...

Duchenne Muscular Dystrophy, or DMD, is a rare and fatal genetic disease that primarily affects boys, slowly robbing them of ...

To help neurologists, clinicians and families understand the current evidence for a new gene therapy for Duchenne muscular dystrophy called delandistrogene moxeparvovec, the American Academy of ...

Muscular dystrophy, known as DMD ... they adopted him despite signs of a muscular disorder — and never looked back. "We're not going to live the rest of our life in fear of what could happen ...

“For nearly a decade, Sarepta has been a leader in advancing the treatment of Duchenne muscular dystrophy through innovative treatment ... and for at least 3 hours after the end of infusion. If ...

Earlier this year, Una Ennis took to social media with a heartfelt plea for funds so she could access specialist treatment abroad, following her seven-year-old son Archie’s muscular dystrophy ...

What is the nervous system? The nervous system is a complex system that controls and coordinates body activities. It's made up of 2 main divisions: Central nervous system. This consists of the brain ...

Duchenne muscular ... dystrophy. It is a progressive genetic disorder that primarily affects boys, leading to gradual muscle degeneration and loss of motor function. In addition to physical ...

Cas12Max-based gene editing therapy for Duchenne muscular dystrophy, one of the most severe forms of the inherited muscular dystrophies that affects primarily boys. Huidagene Therapeutics and ...